therapy-gene-therapy-exagamglogene-autotemcel-sickle-cell

Outcomes

01
biomarker-hematology-hemoglobin-fetal-above-20-percent-at-12-months-achieved-binary-measured
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
02
biomarker-neutrophil-engraftment-duration-days-measured
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
03
biomarker-packed-red-blood-cell-transfusion-units-change-count-measured
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
04
biomarker-platelet-engraftment-duration-days-measured
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
05
oncology-sickle-cell-voc-free-at-12-months-achieved-binary-measured
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
06
oncology-sickle-cell-voc-free-at-12-months-achieved-binary-self-reported
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
07
qol-ankylosing-spondylitis-ascq12-emotional-impact-subscore-self-reported
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
08
qol-ankylosing-spondylitis-ascq12-pain-frequency-subscore-self-reported
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
09
qol-ankylosing-spondylitis-ascq12-pain-impact-subscore-self-reported
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
10
qol-ankylosing-spondylitis-ascq12-pain-severity-subscore-self-reported
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
11
qol-ankylosing-spondylitis-ascq12-sleep-impact-subscore-self-reported
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
12
qol-ankylosing-spondylitis-ascq12-social-functioning-impact-subscore-self-reported
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
13
qol-ankylosing-spondylitis-ascq12-stiffness-impact-subscore-self-reported
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd

therapy-gene-therapy-exagamglogene-autotemcel-sickle-cell

Outcomes

biomarker-hematology-hemoglobin-fetal-above-20-percent-at-12-months-achieved-binary-measured

biomarker-neutrophil-engraftment-duration-days-measured

biomarker-packed-red-blood-cell-transfusion-units-change-count-measured

biomarker-platelet-engraftment-duration-days-measured

oncology-sickle-cell-voc-free-at-12-months-achieved-binary-measured

oncology-sickle-cell-voc-free-at-12-months-achieved-binary-self-reported

qol-ankylosing-spondylitis-ascq12-emotional-impact-subscore-self-reported

qol-ankylosing-spondylitis-ascq12-pain-frequency-subscore-self-reported

qol-ankylosing-spondylitis-ascq12-pain-impact-subscore-self-reported

qol-ankylosing-spondylitis-ascq12-pain-severity-subscore-self-reported

qol-ankylosing-spondylitis-ascq12-sleep-impact-subscore-self-reported

qol-ankylosing-spondylitis-ascq12-social-functioning-impact-subscore-self-reported

qol-ankylosing-spondylitis-ascq12-stiffness-impact-subscore-self-reported