medication-gene-therapy-exagamglogene-autotemcel-sickle-cell-generic

Outcomes

01
biomarker-hemoglobin-fetal-above-20-percent-12-month-achieved-binary-measured
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
02
biomarker-neutrophil-engraftment-duration-days-measured
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
03
biomarker-platelet-engraftment-duration-days-measured
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
04
biomarker-red-blood-cell-transfusion-units-decrease-from-baseline-count-measured
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
05
biomarker-sickle-cell-vaso-occlusive-crisis-free-12-month-binary-self-reported
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
06
biomarker-vaso-occlusive-crisis-free-12-month-binary-measured
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
07
qol-ankylosing-spondylitis-quality-of-life-questionnaire-ascq12-emotional-impact-change-from-baseline-score-self-reported
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
08
qol-ankylosing-spondylitis-quality-of-life-questionnaire-ascq12-pain-episode-frequency-change-from-baseline-score-self-reported
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
09
qol-ankylosing-spondylitis-quality-of-life-questionnaire-ascq12-pain-episode-severity-change-from-baseline-score-self-reported
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
10
qol-ankylosing-spondylitis-quality-of-life-questionnaire-ascq12-pain-impact-change-from-baseline-score-self-reported
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
11
qol-ankylosing-spondylitis-quality-of-life-questionnaire-ascq12-sleep-impact-change-from-baseline-score-self-reported
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
12
qol-ankylosing-spondylitis-quality-of-life-questionnaire-ascq12-social-functioning-impact-change-from-baseline-score-self-reported
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd
13
qol-ankylosing-spondylitis-quality-of-life-questionnaire-ascq12-stiffness-impact-change-from-baseline-score-self-reported
1 evidence row
- exagamglogene-autotemcel-cadth-reimbursement-recommendation_2025_cohort_summary-of-findings-for-exagamglogene-autotemcel-for-patients-with-scd

medication-gene-therapy-exagamglogene-autotemcel-sickle-cell-generic

Outcomes

biomarker-hemoglobin-fetal-above-20-percent-12-month-achieved-binary-measured

biomarker-neutrophil-engraftment-duration-days-measured

biomarker-platelet-engraftment-duration-days-measured

biomarker-red-blood-cell-transfusion-units-decrease-from-baseline-count-measured

biomarker-sickle-cell-vaso-occlusive-crisis-free-12-month-binary-self-reported

biomarker-vaso-occlusive-crisis-free-12-month-binary-measured

qol-ankylosing-spondylitis-quality-of-life-questionnaire-ascq12-emotional-impact-change-from-baseline-score-self-reported

qol-ankylosing-spondylitis-quality-of-life-questionnaire-ascq12-pain-episode-frequency-change-from-baseline-score-self-reported

qol-ankylosing-spondylitis-quality-of-life-questionnaire-ascq12-pain-episode-severity-change-from-baseline-score-self-reported

qol-ankylosing-spondylitis-quality-of-life-questionnaire-ascq12-pain-impact-change-from-baseline-score-self-reported

qol-ankylosing-spondylitis-quality-of-life-questionnaire-ascq12-sleep-impact-change-from-baseline-score-self-reported

qol-ankylosing-spondylitis-quality-of-life-questionnaire-ascq12-social-functioning-impact-change-from-baseline-score-self-reported

qol-ankylosing-spondylitis-quality-of-life-questionnaire-ascq12-stiffness-impact-change-from-baseline-score-self-reported